Seminars

Thursdays from 11:15am-12:30pm
MTRF 3–204 or Zoom

DateSpeakerDepartmentTitle
9/19/2024Lisa Sniderman-KingSanofiProject Searchlight: Using predictive analytics to reduce Gaucher diagnostic delay
10/3/2024Joy SherrickChiesiTreatment considerations for patients with epidermolysis bullosa
10/10/2024Mohamed FayedECPUncovering the Potential of High-Dose Levetiracetam in Neonatal Seizures
10/17/2024John LagusBluestem Pharma Consulting, LLC
Bridging the Access to Medicine Gap for Rare Disease Patients with Expanded Access Programs
10/24/2024Nick MairsDup15q AllianceDup15q overview and opportunities
10/31/2024Jennell BilekCarlson CaspersLife cycle strategies focusing on regulatory exclusivities and patent
11/7/2024Katherine LeeTakeda PharmaceuticalsMechanism of CNS Cholesterol Pathways and TAK-935 (soticlestat)
11/14/2024Marie BradleyFDAAn Overview of FDA’s Real-World Evidence Program
11/28/2024No seminarNo seminarNo seminar
12/12/2024Mohamed DuklefECPBridging Gaps in Rare Disease Care: Global Disparities, Policies, and Progress in Transitioning and Developing Economies