Thursdays from 11:15am-12:30pm
MTRF 3–204 or Zoom
Date | Speaker | Department | Title |
9/19/2024 | Lisa Sniderman-King | Sanofi | Project Searchlight: Using predictive analytics to reduce Gaucher diagnostic delay |
10/3/2024 | Joy Sherrick | Chiesi | Treatment considerations for patients with epidermolysis bullosa |
10/10/2024 | Mohamed Fayed | ECP | Uncovering the Potential of High-Dose Levetiracetam in Neonatal Seizures |
10/17/2024 | John Lagus | Bluestem Pharma Consulting, LLC | Bridging the Access to Medicine Gap for Rare Disease Patients with Expanded Access Programs |
10/24/2024 | Nick Mairs | Dup15q Alliance | Dup15q overview and opportunities |
10/31/2024 | Jennell Bilek | Carlson Caspers | Life cycle strategies focusing on regulatory exclusivities and patent |
11/7/2024 | Katherine Lee | Takeda Pharmaceuticals | Mechanism of CNS Cholesterol Pathways and TAK-935 (soticlestat) |
11/14/2024 | Marie Bradley | FDA | An Overview of FDA’s Real-World Evidence Program |
11/28/2024 | No seminar | No seminar | No seminar |
12/12/2024 | Mohamed Duklef | ECP | Bridging Gaps in Rare Disease Care: Global Disparities, Policies, and Progress in Transitioning and Developing Economies |